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72 results
Type : Drugs, devices and medical acts
Topics : Metabolic diseases
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Date
POMBILITI (cipaglucosidase alfa)
Medicine
- Posted on 09/11/2023
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Evaluation of the METAglut1™ test in the diagnosis of glucose transporter type 1 deficiency syndrome - INAHTA Brief
Health technology assessment
- Posted on 27/04/2023
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document
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my selection
BICAFRES (bicarbonate de sodium)
Medicine
- Posted on 10/02/2023
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AMVUTTRA (vutrisiran)
Medicine
- Posted on 05/04/2024
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EVKEEZA (évinacumab)
Medicine
- Posted on 06/05/2024
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NEXVIADYME (avalglucosidase alfa)
Medicine
- Posted on 12/10/2023
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OXLUMO (lumasiran)
Medicine
- Posted on 24/09/2021
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PALYNZIQ (pegvaliase)
Medicine
- Posted on 02/12/2020
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VYNDAQEL
Medicine
- Posted on 16/10/2020 - Mis à jour le 16/10/2020
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MIACALCIC
Medicine
- Posted on 02/10/2020 - Mis à jour le 2/10/2020
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PROLASTIN
Medicine
- Posted on 08/03/2024
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MEPSEVII
Medicine
- Posted on 01/07/2020 - Mis à jour le 1/7/2020
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GIVLAARI
Medicine
- Posted on 01/04/2021
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Clinical usefulness of vitamin B1 testing - INAHTA Brief
Health technology assessment
- Posted on 22/03/2021
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document
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RENVELA
Medicine
- Posted on 18/03/2020 - Mis à jour le 18/3/2020
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CUFENCE (trientine dichlorhydrate)
Medicine
- Posted on 25/01/2024
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WAYLIVRA (volanesorsen)
Medicine
- Posted on 12/03/2020
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ADENURIC (fébuxostat)
Medicine
- Posted on 04/03/2020 - Mis à jour le 4/3/2020
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EZETROL (ézétimibe)
Medicine
- Posted on 09/12/2019 - Mis à jour le 9/12/2019
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ILARIS
Medicine
- Posted on 18/09/2024
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TEGSEDI
Medicine
- Posted on 30/09/2019
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CRESTOR (rosuvastatine calcique)
Medicine
- Posted on 02/04/2020
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MYALEPTA (métréleptine)
Medicine
- Posted on 07/06/2019 - Mis à jour le 12/6/2019
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SIGNIFOR (pasiréotide)
Medicine
- Posted on 12/03/2019 - Mis à jour le 12/6/2019
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my selection
CUPRIOR (trientine (tétrachlorhydrate de))
Medicine
- Posted on 11/06/2019 - Mis à jour le 12/6/2019
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VELTASSA (patiromer), résine échangeuse de cations
Medicine
- Posted on 05/10/2022
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CRYSVITA
Medicine
- Posted on 25/01/2024
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LAMZEDE (velmanase alfa)
Medicine
- Posted on 08/06/2022
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REPATHA
Medicine
- Posted on 18/04/2024
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SAMSCA (tolvaptan)
Medicine
- Posted on 18/12/2018 - Mis à jour le 12/6/2019
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my selection
FIRAZYR (icatibant (acétate d'))
Medicine
- Posted on 08/02/2019 - Mis à jour le 12/6/2019
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PROCYSBI (mercaptamine (bitartrate de))
Medicine
- Posted on 29/08/2018 - Mis à jour le 12/6/2019
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MIMPARA (cinacalcet (chlorhydrate de))
Medicine
- Posted on 28/11/2018 - Mis à jour le 12/6/2019
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RAVICTI (phénylbutyrate de glycérol)
Medicine
- Posted on 05/09/2019
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ZURAMPIC (lésinurad)
Medicine
- Posted on 24/10/2018 - Mis à jour le 12/6/2019
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DUPHALAC (lactulose)
Medicine
- Posted on 09/04/2021
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