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165 results
Type : Drugs, devices and medical acts
Topics : Congenital, genetic and rare diseases
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Title
Date
VYVGART (efgartigimod alfa)
Medicine
- Posted on 01/08/2024 - Mis à jour le 1/8/2024
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CAMZYOS (mavacamten)
Medicine
- Posted on 09/11/2023
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ENJAYMO (sutimlimab)
Medicine
- Posted on 08/09/2023
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POMBILITI (cipaglucosidase alfa)
Medicine
- Posted on 09/11/2023
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Comparative genomic hybridization array (CGHA) analysis in postnatal context - INAHTA Brief
Health technology assessment
- Posted on 20/07/2023
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document
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Evaluation of the METAglut1™ test in the diagnosis of glucose transporter type 1 deficiency syndrome - INAHTA Brief
Health technology assessment
- Posted on 27/04/2023
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document
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CEVENFACTA (eptacog bêta - FVIIa)
Medicine
- Posted on 27/01/2023
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AMVUTTRA (vutrisiran)
Medicine
- Posted on 05/04/2024
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EVKEEZA (évinacumab)
Medicine
- Posted on 06/05/2024
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FILSUVEZ (extrait sec raffiné d’écorce de bouleau)
Medicine
- Posted on 03/02/2023
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FLUDROCORTISONE ACETATE ACCORD (acétate de fludrocortisone)
Medicine
- Posted on 13/10/2022
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NEXVIADYME (avalglucosidase alfa)
Medicine
- Posted on 12/10/2023
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TECEOS (butédronate)
Medicine
- Posted on 29/07/2022
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ENSPRYNG (satralizumab)
Medicine
- Posted on 10/02/2022
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ORLADEYO (dichlorhydrate de bérotralstat)
Medicine
- Posted on 08/12/2021
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ONTOZRY (cénobamate)
Medicine
- Posted on 28/06/2023
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EVRYSDI (risdiplam)
Medicine
- Posted on 30/09/2021
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OXLUMO (lumasiran)
Medicine
- Posted on 24/09/2021
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ELZONRIS (tagraxofusp)
Medicine
- Posted on 26/08/2021
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COAGADEX (facteur X de coagulation humain)
Medicine
- Posted on 24/09/2021
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REBLOZYL (luspatercept)
Medicine
- Posted on 25/01/2024
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FINTEPLA (fenfluramine)
Medicine
- Posted on 03/06/2021
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ADAKVEO (crizanlizumab)
Medicine
- Posted on 07/05/2021
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ISTURISA (osilodrostat)
Medicine
- Posted on 07/05/2021
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LIBMELDY 2-10 x 106 cellules/ml dispersion pour perfusion (atidarsagène autotemcel)
Medicine
- Posted on 20/10/2022
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XROMI (hydroxycarbamide)
Medicine
- Posted on 09/04/2021
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AYVAKYT (avapritinib)
Medicine
- Posted on 05/09/2024
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ESPEROCT (turoctocog alfa pégol)
Medicine
- Posted on 11/03/2021
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BESREMI (ropeginterféron alfa-2b)
Medicine
- Posted on 23/12/2020
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ZOLGENSMA (onasemnogene abeparvovec)
Medicine
- Posted on 25/05/2023
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PALYNZIQ (pegvaliase)
Medicine
- Posted on 02/12/2020
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KAFTRIO / KALYDECO
Medicine
- Posted on 17/05/2024
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VYNDAQEL
Medicine
- Posted on 16/10/2020 - Mis à jour le 16/10/2020
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LUCENTIS
Medicine
- Posted on 19/10/2021
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SYLVANT
Medicine
- Posted on 02/10/2020 - Mis à jour le 2/10/2020
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MIACALCIC
Medicine
- Posted on 02/10/2020 - Mis à jour le 2/10/2020
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