Clinical Benefit
| Substantial |
Le service médical rendu par cette spécialité est important dans le traitement au long cours des patients atteints du syndrome de Hunter (mucopolysaccharidose de type II).
|
Clinical Added Value
| important |
ELAPRASE, première thérapie de substitution enzymatique dans le traitement du syndrome de Hunter, apporte une amélioration du service médical rendu importante (ASMR II).
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