Autorisation d’accès précoce refusée à la spécialité EMCITATE (tiratricol) dans l'indication « traitement de la thyrotoxicose périphérique chez les patients atteints d’un déficit en transporteur 8 de monocarboxylate (MCT8) (syndrome d’Allan-Herndon-Dudley), dès la naissance. »
See also
HAS opinions and decisions
07/08/2025
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